FDA awards ODD status to Sanofi's rilzabrutinib for two rare conditions

By Yahoo! Finance   |   3 weeks ago
FDA awards ODD status to Sanofi's rilzabrutinib for two rare conditions

Sanofi's rilzabrutinib, a BTK inhibitor, received FDA orphan drug designation for treating IgG4-related disease and warm autoimmune haemolytic anaemia. Promising results from Phase II trials show potential benefits for patients.

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